GENE THERAPY

• gene therapy is used to treat genetic diseases caused by mutations in single genes, such as cystic fibrosis or sickle-cell anaemia.
• gene therrapy and cell replacement therapy

  stem cells taken from patient

  • mutant gene replaced with normal gene
  • cells multiplied
  • cells transferred back to patient
• what is cell replacement therapy

  transplanting stem cells into a patient
• what is gene therapy?

  removing faulty genes and replacing with healthy genes